World's most expensive medicine treats infants with genetic disorder

World’s most expensive medicine treats infants with genetic disorder


A baby boy has become one of the first patients to be treated on the UK’s NHS with Zolgensma, the world’s most expensive medicine.

Little Arthur is one of around 40 children are born with the most severe form of Spinal Muscular Atrophy (SMA) every year.

The gene therapy has a list price of about $2.5m and is manufactured by Novartis Gene Therapies.

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